Ace the Case: A 28-Year-Old Man With Hepatomegaly and Dyslipidemia
There is no commercial support for this activity.
You passed! Review the answers below.
Please try again. The questions you answered incorrectly are highlighted in red below.
Correct answer: D.
Rationale: Sebelipase alpha is a recombinant lysosomal lipase, FDA approved in December 2015 to treat lysosomal acid lipase deficiency in infants and adults.11 It is administered once a week via intravenous infusion in people with rapidly progressing disease in the first 6 months of life, and every other week with less aggressive disease.11